CAN 201
Alternative Names: CAN-201Latest Information Update: 28 May 2025
At a glance
- Originator CANbridge Pharmaceuticals
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Fabry's disease
Most Recent Events
- 28 May 2025 No recent reports of development identified for preclinical development in Fabry's-disease in China (Parenteral)
- 26 Oct 2023 Pharmacodynamics and safety data from a preclinical studies in Fabry's disease released by CANbridge Pharmaceuticals
- 03 Jan 2023 CANbridge Pharmaceuticals completed adeno-associated virus (AAV) sL65 based capsid technology transfer from LogicBio Therapeutics