VY HTT01
Alternative Names: Huntington's disease gene therapy - Voyager Therapeutics; VY-HTT01Latest Information Update: 31 Mar 2022
At a glance
- Originator Voyager Therapeutics
- Class Antiparkinsonians; Gene therapies; Neuroprotectants
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
- Available For Licensing Yes
Highest Development Phases
- Discontinued Huntington's disease