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Research programme: gene therapies - Allen Institute/BioMarin Pharmaceuticals

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Research programme: gene therapies - Allen Institute/BioMarin Pharmaceuticals

Latest Information Update: 23 Apr 2024

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At a glance

  • Originator Allen Institute
  • Developer Allen Institute; BioMarin Pharmaceutical
  • Class Gene therapies
  • Mechanism of Action Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • Preclinical CNS disorders

Most Recent Events

  • 23 Apr 2024 Preclinical trials in CNS disorders in USA (Parenteral) before April 2024 (BioMarin Pharmaceuticals pipeline, April 2024)
  • 28 Apr 2021 Allen Institute and BioMarin Pharmaceuticals collaborate to develop gene therapies for CNS disorders
  • 28 Apr 2021 Early research in CNS disorders in USA (Parenteral)

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