Either you have JavaScript disabled or your browser does not support Javascript . To work properly, this page requires JavaScript to be enabled.
How to enable JavaScript in your browser?

GT 02287

Next Previous
Drug Profile

GT 02287

Alternative Names: GT-02287

Latest Information Update: 25 Mar 2026

Price :
$50 *
Note:
  • Adis is an information provider. We do not sell or distribute actual drugs.
  • Final gross price and currency may vary according to local VAT and billing address.
  • Your purchase entitles you to full access to the information contained in our drug profile at the time of purchase.
  • A link to download a PDF version of the drug profile will be included in your email receipt.

At a glance

  • Originator Gain Therapeutics
  • Class Antidementias; Antineoplastics; Antiparkinsonians; Neuroprotectants; Pharmacological chaperones; Small molecules
  • Mechanism of Action Galactosylceramidase modulators
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity Yes

Highest Development Phases

  • Phase I Parkinson's disease
  • Preclinical Gaucher's disease; Solid tumours
  • Research Dementia
  • Discontinued Alpha 1-antitrypsin deficiency; Globoid cell leukodystrophy; GM1 gangliosidosis

Most Recent Events

  • 12 Mar 2026 Gain Therapeutics submits IND application of GT 02287 in Parkinson's disease to US FDA
  • 12 Mar 2026 Gain Therapeutics submits response to US FDA’s request for additional preclinical data
  • 12 Mar 2026 Gain Therapeutics plans a phase II trial for Parkinson's disease in Q3 2026

You need to be a logged in or subscribed to view this content

Request demo (opens in a new window)
If your organization or you do not have a subscription, try one of the following: If your organization has a subscription, there are several access options, even while working remotely:
  • Working within your organization’s network
  • with username/password or try to via your institution
  • Persisted access using your organization’s identifier stored in your user browser for 90 days
Back to top