GT 02287
Alternative Names: GT-02287Latest Information Update: 02 Sep 2024
At a glance
- Originator Gain Therapeutics
- Class Antidementias; Antineoplastics; Antiparkinsonians; Neuroprotectants; Pharmacological chaperones; Small molecules
- Mechanism of Action Alpha 1-antitrypsin modulators; Galactosidase modulators; Galactosylceramidase modulators; Glucosylceramidase stimulants
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I Parkinson's disease
- Preclinical Alpha 1-antitrypsin deficiency; Gaucher's disease; Globoid cell leukodystrophy; GM1 gangliosidosis; Solid tumours
- Research Dementia
Most Recent Events
- 29 Aug 2024 Pharmacodynamics and adverse event data from a phase I trial in Parkinson's disease released by Gain Therapeutics
- 09 Jul 2024 Adverse events and pharmacokinetics data from a phase I trial in Parkinsons disease released by Gain Therapeutics
- 27 Jun 2024 Pharmacodynamics data from a preclinical trial in Parkinson's disease released by Gain Therapeutics