GLB 2001
Alternative Names: AAV8.pXLLY027Latest Information Update: 28 Jun 2025
At a glance
- Originator GeneLeap Biotech
- Class Blood coagulation factors; Gene therapies
- Mechanism of Action Factor IX replacements; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Haemophilia B
Most Recent Events
- 28 Jun 2025 No recent reports of development identified for preclinical development in Haemophilia-B in USA
- 14 May 2021 Preclinical trials in Haemophilia B in USA (unspecified route) as of May 2021 (Company pipeline)