SGT 003
Alternative Names: SGT-003Latest Information Update: 19 Nov 2025
At a glance
- Originator Solid Biosciences
- Class Gene therapies
- Mechanism of Action Dystrophin replacements; Gene transference
-
Orphan Drug Status
Yes - Duchenne muscular dystrophy
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase III Duchenne muscular dystrophy
Most Recent Events
- 06 Nov 2025 Solid Biosciences announces intention to commercialize SGT 003 for Duchenne muscular dystrophy in the UK
- 06 Nov 2025 Solid Biosciences announces intention to collaborate closely with the UK MHRA for the further development of SGT 003
- 06 Nov 2025 Solid Biosciences receives innovation passport designation under the new UK innovative licensing and access pathway for SGT 003