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RP A701

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Drug Profile

RP A701

Alternative Names: REN-001 - Rocket Pharmaceuticals; RP-A701

Latest Information Update: 16 Apr 2026

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At a glance

  • Originator Renovacor
  • Developer Rocket Pharmaceuticals
  • Class Cardiovascular therapies; Gene therapies
  • Mechanism of Action BAG3 protein replacements; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • Phase I Dilated cardiomyopathy

Most Recent Events

  • 29 Mar 2026 Phase-I clinical trials in Dilated cardiomyopathy in USA (IV) (NCT07137338)
  • 13 Nov 2025 RP A701 is still in preclinical development in Dilated cardiomyopathy in USA (Intracoronary)
  • 28 Oct 2025 No recent reports of development identified for preclinical development in Dilated cardiomyopathy in USA (Intracoronary)

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