Either you have JavaScript disabled or your browser does not support Javascript . To work properly, this page requires JavaScript to be enabled.
How to enable JavaScript in your browser?

RP A701

Next Previous
Drug Profile

RP A701

Alternative Names: REN-001 - Rocket Pharmaceuticals; RP-A701

Latest Information Update: 21 Aug 2025

Price :
$50 *
Note:
  • Adis is an information provider. We do not sell or distribute actual drugs.
  • Final gross price and currency may vary according to local VAT and billing address.
  • Your purchase entitles you to full access to the information contained in our drug profile at the time of purchase.
  • A link to download a PDF version of the drug profile will be included in your email receipt.

At a glance

  • Originator Renovacor
  • Developer Rocket Pharmaceuticals
  • Class Cardiovascular therapies; Gene therapies
  • Mechanism of Action BAG3 protein replacements; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • Preclinical Dilated cardiomyopathy

Most Recent Events

  • 07 Aug 2025 RP A701 receives Fast Track designation for Dilated cardiomyopathy [Intracoronary] in USA
  • 03 Jul 2025 Rocket Pharmaceuticals plans phase I trial in Dilated cardiomyopathy in USA
  • 30 Jun 2025 The US FDA approves IND application for RP A701 in Dilated cardiomyopathy

You need to be a logged in or subscribed to view this content

Request demo (opens in a new window)
If your organization or you do not have a subscription, try one of the following: If your organization has a subscription, there are several access options, even while working remotely:
  • Working within your organization’s network
  • with username/password or try to via your institution
  • Persisted access using your organization’s identifier stored in your user browser for 90 days
Back to top