Either you have JavaScript disabled or your browser does not support Javascript . To work properly, this page requires JavaScript to be enabled.
How to enable JavaScript in your browser?

Research programme: in vivo gene editing therapies - Capsida Biotherapeutics/CRISPR Therapeutics

Next Previous
X
Search
Drug Profile

Research programme: in vivo gene editing therapies - Capsida Biotherapeutics/CRISPR Therapeutics

Latest Information Update: 24 Mar 2022

Price : $50 *
  • Adis is an information provider. We do not sell or distribute actual drugs.
  • Final gross price and currency may vary according to local VAT and billing address.
  • Your purchase entitles you to full access to the information contained in our drug profile at the time of purchase.
  • A link to download a PDF version of the drug profile will be included in your email receipt.

At a glance

  • Originator Capsida Biotherapeutics; CRISPR Therapeutics
  • Class Gene therapies
  • Mechanism of Action Gene modulators
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • Research Amyotrophic lateral sclerosis; Friedreich's ataxia

Most Recent Events

  • 24 Mar 2022 Capsida Biotherapeutics has patent protection for Adeno-associated virus compositions for targeted gene therapy in the US
  • 15 Jun 2021 CRISPR Therapeutics and Capsida Biotherapeutics agree to co-promote and co-develop in vivo gene editing therapies for Amyotrophic lateral sclerosis and Friedreich’s ataxia
  • 15 Jun 2021 Early research in Amyotrophic lateral sclerosis in USA (Parenteral)

You need to be a logged in or subscribed to view this content Request demo

If your organization or you do not have a subscription, try one of the following:
  • Contacting your organization’s admin about adding this content to your AdisInsight subscription
  • Buying a PDF version of any individual profile
  • Request a free trial
If your organization has a subscription, there are several access options, even while working remotely:
  • Working within your organization’s network
  • with username/password or try to via your institution
  • Persisted access using your organization’s identifier stored in your user browser for 90 days
Back to top