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Research programme: lysosomal storage disorder therapeutics - Cellectis

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Drug Profile

Research programme: lysosomal storage disorder therapeutics - Cellectis

Alternative Names: Research programme: LSD TALEN-based therapeutics - Cellectis

Latest Information Update: 28 Jul 2025

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At a glance

  • Originator Cellectis
  • Class Gene therapies
  • Mechanism of Action Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • No development reported Lysosomal storage diseases

Most Recent Events

  • 28 Jul 2025 No recent reports of development identified for research development in Lysosomal storage diseases in France (Parenteral)
  • 14 Jun 2021 Early research in Lysosomal storage diseases in France (Parenteral) prior to June 2021

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