Research programme: recombination activating gene 1 severe combined immunodeficiency gene therapies - Cellectis/University of Freiburg
Alternative Names: Research programme: RAG1 SCID gene therapies - Cellectis; Research programme: RAG1 severe combined immunodeficiency gene therapies - CellectisLatest Information Update: 06 Jul 2021
At a glance
- Originator Cellectis
- Developer Cellectis; University of Freiburg
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Severe combined immunodeficiency
Most Recent Events
- 14 Jun 2021 Early research in Severe-combined-immunodeficiency in France (Parenteral) prior to June 2021
- 14 Jun 2021 Early research in Severe-combined-immunodeficiency in Germany (Parenteral) prior to June 2021
- 14 Jun 2021 Pharmacodynamics data from research studies in Severe-combined-immunodeficiency released by Cellectis