VTA 100
Alternative Names: VTA-100Latest Information Update: 28 Mar 2022
At a glance
- Originator Vita Therapeutics
- Class Gene therapies; Induced pluripotent stem cell therapies
- Mechanism of Action Cell replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Limb girdle muscular dystrophy type 2A
Most Recent Events
- 22 Mar 2022 Vita Therapeutics expects to file an IND application with the US FDA for Limb-girdle-muscular-dystrophy in 2023
- 23 Jun 2021 Vita Therapeutics plans a clinical trial for Limb girdle muscular dystrophy type 2A
- 23 Jun 2021 Preclinical trials in Limb girdle muscular dystrophy type 2A in USA (Parenteral)