VTA 200
Alternative Names: VTA-200Latest Information Update: 18 Apr 2025
At a glance
- Originator Vita Therapeutics
- Class Gene therapies; Induced pluripotent stem cell therapies
- Mechanism of Action Cell replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Muscular dystrophies
Most Recent Events
- 08 Apr 2025 Vita Therapeutics in-licenses hfCas12Max CRISPR technology from Synthego for development of their hypoimmunogenic cell therapies for neuromuscular disorders
- 23 Jun 2021 Early research in Muscular dystrophies in USA (Parenteral) before June 2021
- 27 May 2021 Vita Therapeutics has patents pending for hypoimmunogenic muscle precursor cells worldwide