Research programme: Immunological disorders - Apellis Pharmaceuticals/Beam Therapeutics
Latest Information Update: 28 Jul 2025
At a glance
- Originator Apellis Pharmaceuticals; Beam Therapeutics
- Class Gene therapies
- Mechanism of Action Complement C3 modulators; Gene modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Immunological disorders
Most Recent Events
- 28 Jul 2025 No recent reports of development identified for preclinical development in Immunological-disorders in USA
- 30 Jun 2021 Apellis Pharmaceuticals and Beam Therapeutics enters into an five-year research collaboration agreement to discover new treatments for complement-driven diseases
- 30 Jun 2021 Preclinical development in Immunological disorders in USA