Research programme: Immunological disorders - Apellis Pharmaceuticals/Beam Therapeutics
Latest Information Update: 04 Aug 2021
At a glance
- Originator Apellis Pharmaceuticals; Beam Therapeutics
- Class Gene therapies
- Mechanism of Action Complement C3 modulators; Gene modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Immunological disorders