GT DF 100
Alternative Names: Dysferlin gene therapy - Genotarget; GT DF-100Latest Information Update: 22 Jul 2021
Price :
$50 *
At a glance
- Originator Genotarget
- Class Gene therapies
- Mechanism of Action Dysferlin replacements; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Limb girdle muscular dystrophies
Most Recent Events
- 21 Jul 2021 Preclinical trials in Limb girdle muscular dystrophies in Russia (Parenteral) before July 2021 (Genotarget pipeline, July 2021)