GT CN 100
Alternative Names: Calpain gene therapy - Genotarget; GT CN-100Latest Information Update: 22 Jul 2021
At a glance
- Originator Genotarget
- Class Gene therapies
- Mechanism of Action Calpain replacements; Gene transference
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Limb girdle muscular dystrophies
Most Recent Events
- 21 Jul 2021 Early research in Limb girdle muscular dystrophies in Russia (Parenteral) before July 2021 (Genotarget pipeline, July 2021)