Research programme: adeno-associated viral gene therapies - Coave Therapeutics
Latest Information Update: 03 May 2024
At a glance
- Originator Coave Therapeutics
- Developer Coave Therapeutics; Institute of Neurodegenerative Diseases
- Class Antiparkinsonians; Gene therapies; Neuroprotectants
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical CNS disorders; Eye disorders; Multiple system atrophy; Parkinson's disease
Most Recent Events
- 30 Apr 2024 Interim pharmacodynamics data from a preclinical studies in eye disorders released by Coave Therapeutics
- 14 Sep 2022 Coave Therapeutics and Institute of Neurodegenerative Diseases enter into a collaboration to develop adeno-associated viral gene therapies in France for Multiple system atrophy and Parkinson's disease .
- 14 Sep 2022 Preclinical trials in Multiple system atrophy in France (unspecified route)