LX 2022
Alternative Names: LX-2022; TNNI3 HCM - LEXEO TherapeuticsLatest Information Update: 11 Aug 2021
At a glance
- Originator Stelios Therapeutics
- Developer LEXEO Therapeutics
- Class Cardiovascular therapies; Gene therapies
- Mechanism of Action Gene transference
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Hypertrophic cardiomyopathy