Research programme: gene therapy - University of Sheffield
Latest Information Update: 28 Aug 2025
At a glance
- Originator University of Sheffield
- Class Antidementias; Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Frontotemporal dementia; Motor neuron disease
Most Recent Events
- 28 Aug 2025 No recent reports of development identified for research development in Frontotemporal dementia in United Kingdom (Parenteral)
- 28 Aug 2025 No recent reports of development identified for research development in Motor-neuron-disease in United Kingdom (Parenteral)
- 01 Jul 2021 Early research in Frontotemporal dementia in United Kingdom (Parenteral)