Research programme: gene therapy - University of Sheffield
Latest Information Update: 11 Aug 2021
At a glance
- Originator University of Sheffield
- Class Antidementias; Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Frontotemporal dementia; Motor neuron disease