Research programme: chaperone therapy - GC Biopharma/Tottori University
Latest Information Update: 28 Sep 2025
At a glance
- Originator Tottori University
- Developer GC Biopharma; Tottori University
- Class Pharmacological chaperones; Small molecules
- Mechanism of Action Glycoside hydrolase modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Gangliosidoses
Most Recent Events
- 28 Sep 2025 No recent reports of development identified for research development in Gangliosidoses in Japan (PO)
- 28 Sep 2025 No recent reports of development identified for research development in Gangliosidoses in South Korea (PO)
- 29 Mar 2022 GC Pharma is now called GC Biopharma