Dalnacogene ponparvovec - Belief Biomed
Alternative Names: BBM-H901Latest Information Update: 28 Apr 2026
At a glance
- Originator Belief Biomed
- Developer Belief Biomed; Takeda China
- Class Antihaemorrhagics; Gene therapies
- Mechanism of Action Factor IX replacements; Gene transference
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Orphan Drug Status
Yes - Haemophilia B
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Marketed Haemophilia B