APL 1030 gene therapy - Apellis Pharmaceuticals
Alternative Names: APL-1030 gene therapyLatest Information Update: 27 Aug 2021
At a glance
- Originator Apellis Pharmaceuticals
- Class Gene therapies; Neuroprotectants
- Mechanism of Action Complement C3 inhibitors; Complement C3b inactivator protein inhibitors; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Neurodegenerative disorders
Most Recent Events
- 30 Jun 2021 Preclinical trials in Neurodegenerative disorders in USA (parenteral)