Non-viral gene therapy - Myosana Therapeutics
Latest Information Update: 28 Sep 2025
At a glance
- Originator Myosana Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Duchenne muscular dystrophy
Most Recent Events
- 28 Sep 2025 No recent reports of development identified for research development in Duchenne muscular dystrophy in USA (Parenteral)
- 26 Aug 2021 Early research in Duchenne muscular dystrophy in USA (Parenteral)