Research programme: transcription factor EB activators - Generian Pharmaceuticals
Alternative Names: TFEB modulators - Generian PharmaceuticalsLatest Information Update: 01 Mar 2024
At a glance
- Originator Generian Pharmaceuticals
- Class Eye disorder therapies; Small molecules
- Mechanism of Action TFEB protein stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Preclinical Dry age-related macular degeneration
- Discontinued Lysosomal storage diseases; Unspecified
Most Recent Events
- 12 Feb 2024 Preclinical trials in Dry age-related macular degeneration in USA (unspecified route) before February 2024 (Generian Pharmaceuticals pipeline, February 2024)
- 12 Feb 2024 Transcription factor EB activators are available for licensing as of 12 Feb 2024. https://www.generian.com/pipeline/ (Generian Pharmaceuticals pipeline, February 2024)
- 25 Mar 2023 Discontinued - Preclinical for Lysosomal storage diseases in USA (unspecified route) before March 2023 (Generian Pharmaceuticals pipeline, March 2023)