Research programme: small interfering RNA-based therapeutics - Alnylam Pharmaceuticals/Novartis
Alternative Names: Research programme: siRNA-based therapeutics - Alnylam Pharmaceuticals/NovartisLatest Information Update: 28 Feb 2026
At a glance
- Originator Alnylam Pharmaceuticals; Novartis
- Class Small interfering RNA
- Mechanism of Action RNA interference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Liver failure
Most Recent Events
- 28 Feb 2026 No recent reports of development identified for research development in Liver-failure in USA (Parenteral)
- 06 Jan 2022 Alnylam enters into R&D agreement with Novartis for siRNA-based targeted therapy for liver failure/end-stage liver disease (ESLD)
- 06 Jan 2022 Early research in Liver failure in USA (Parenteral)