Research programme: small interfering RNA-based therapeutics - Alnylam Pharmaceuticals/Novartis
Alternative Names: Research programme: siRNA-based therapeutics - Alnylam Pharmaceuticals/NovartisLatest Information Update: 24 Jan 2022
At a glance
- Originator Alnylam Pharmaceuticals; Novartis
- Class Small interfering RNA
- Mechanism of Action RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Liver failure