Research programme: dentatorubral-pallidoluysian atrophy therapeutics - Quiver Bioscience
Latest Information Update: 28 May 2025
At a glance
- Originator Q-State Biosciences
- Developer Quiver Bioscience
- Class Antiepileptic drugs; Antisense oligonucleotides
- Mechanism of Action RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Myoclonic epilepsies