Research programme: AAV gene therapies - Pfizer
Alternative Names: AAV-delivered gene therapies for Cardiovascular disorders - Pfizer; AAV-delivered gene therapies for Neurological disorders - PfizerLatest Information Update: 19 Mar 2025
At a glance
- Originator Pfizer
- Class Cardiovascular therapies; Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Cardiovascular disorders; Neurological disorders
Most Recent Events
- 05 Oct 2022 Pfizer exercises its option to license a of Next-Generation AAV Capsid for Rare Neurologic Disease Target
- 03 May 2022 Pharmacodynamics data from a preclinical trial in Cardiovascular disorders and Neurological disorders released by Voyager Therapeutics
- 06 Oct 2021 Pfizer in-licenses TRACERᵀᴹ technology from Voyager Therapeutics