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Research programme: lysosomal storage disorder therapeutics - M6P Therapeutics

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Drug Profile

Research programme: lysosomal storage disorder therapeutics - M6P Therapeutics

Latest Information Update: 15 Feb 2022

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At a glance

  • Originator M6P Therapeutics
  • Class Enzymes; Gene therapies
  • Mechanism of Action Enzyme replacements; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity Yes

Highest Development Phases

  • Research Neuronal ceroid lipofuscinosis

Most Recent Events

  • 10 Feb 2022 Pharmacodynamics data from preclinical trial presented at the 18th Annual WORLDSymposium™ (Annual WORLDSymposium-2022)
  • 08 Oct 2021 Early research in Neuronal ceroid lipofuscinosis in USA (unspecified route) before October 2021
  • 08 Oct 2021 Pharmacodynamics data from preclinical trials in Neuronal ceroid lipofuscinosis released by M6P Therapeutics

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