CCB 001
Alternative Names: CCB-001Latest Information Update: 28 Nov 2025
At a glance
- Originator Mayo Clinic
- Developer Castle Creek Pharmaceuticals
- Class Gene therapies
- Mechanism of Action Gene transference
-
Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Osteogenesis imperfecta
Most Recent Events
- 28 Nov 2025 No recent reports of development identified for research development in Osteogenesis-imperfecta in USA
- 13 Oct 2021 Mayo Clinic out-licenses CCB 001 to Castle Creek Pharmaceuticals to advance discovery and pre-clinical development in Osteogenesis imperfecta
- 13 Oct 2021 Early research in Osteogenesis imperfecta in USA (unspecified route)