CCB 003
Alternative Names: CCB-003Latest Information Update: 28 Nov 2025
At a glance
- Originator Mayo Clinic
- Developer Castle Creek Pharmaceuticals
- Class Gene therapies
- Mechanism of Action Gene transference
-
Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Ehlers-Danlos syndrome
Most Recent Events
- 28 Nov 2025 No recent reports of development identified for research development in Ehlers-Danlos-syndrome in USA
- 13 Oct 2021 Mayo Clinic out-licenses CCB 003 to Castle Creek Pharmaceuticals to advance discovery and pre-clinical development in Ehlers-Danlos syndrome
- 13 Oct 2021 Early research in Ehlers-Danlos syndrome in USA (unspecified route)