CLN7 disease gene therapy - Taysha Gene Therapies/University of Texas Southwestern Medical Center
Latest Information Update: 10 Nov 2021
At a glance
- Originator University of Texas Southwestern Medical Center
- Developer Taysha Gene Therapies; University of Texas Southwestern Medical Center
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Neuronal ceroid lipofuscinosis
Most Recent Events
- 05 Oct 2021 University of Texas Southwestern Medical Center and Taysha Gene Therapies agree to co-develop next gereration CLN7 disease gene therapy for Neuronal ceroid lipofuscinosis
- 05 Oct 2021 Preclinical trials in Neuronal ceroid lipofuscinosis in USA (Intrathecal)
- 05 Oct 2021 Taysha Gene Therapies plans a clinical trial in Neuronal ceroid lipofuscinosis in 2022