Drug Profile

Research programme: genetic disorder therapeutics - BridgeBio Pharma/ Columbia University/Mount Sinai Health System

Latest Information Update: 28 Nov 2025

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At a glance

Orphan Drug Status

Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

No
New Molecular Entity Yes

28 Nov 2025 No recent reports of development identified for research development in Cancer in USA
28 Nov 2025 No recent reports of development identified for research development in Inborn genetic disorders in USA
29 Oct 2021 BridgeBio Pharma enters into R&D agreement with Columbia University for Inborn genetic disorders and Cancer

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