Research programme: genetic disorder therapeutics - BridgeBio Pharma/ Columbia University/Mount Sinai Health System
Latest Information Update: 15 Nov 2021
At a glance
- Originator BridgeBio Pharma; Columbia University; Mount Sinai Health System
- Class Antineoplastics
- Mechanism of Action Undefined mechanism
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Cancer; Inborn genetic disorders
Most Recent Events
- 29 Oct 2021 BridgeBio Pharma enters into R&D agreement with Columbia University for Inborn genetic disorders and Cancer
- 29 Oct 2021 BridgeBio Pharma enters into R&D agreement with Mount Sinai Health System for Inborn genetic disorders and Cancer
- 29 Oct 2021 Early research in Cancer in USA (unspecified route)