BMD 001
Alternative Names: BMD-001Latest Information Update: 08 Jun 2023
At a glance
- Originator BIORCHESTRA
- Class Antidementias; Antiparkinsonians; Antisense oligonucleotides; Neuroprotectants
- Mechanism of Action MicroRNA inhibitors; RNA interference
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Alzheimer's disease; Amyotrophic lateral sclerosis; Parkinson's disease
- Discontinued Huntington's disease; Neurodegenerative disorders; Unspecified