ENTR 601 44
Alternative Names: ENTR-601-44; Exon 44 Skipping Oligonucleotide - Entrada TherapeuticsLatest Information Update: 19 Jan 2026
At a glance
- Originator Entrada Therapeutics
- Class Drug conjugates; Oligonucleotides
- Mechanism of Action Nucleic acid modulators
-
Orphan Drug Status
Yes - Duchenne muscular dystrophy
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I/II Duchenne muscular dystrophy
Most Recent Events
- 09 Jan 2026 ENTR 601 44 receives Rare Pediatric Disease Designation for Duchenne muscular dystrophy in USA
- 30 Jun 2025 Phase-I/II clinical trials in Duchenne muscular dystrophy (In adolescents, In children, In adults) in United Kingdom (IV) (NCT07037862)
- 30 Jun 2025 Phase-I/II clinical trials in Duchenne muscular dystrophy (In children, In adolescents, In adults) in Spain, Belgium (IV) (NCT07037862)