Research programme: small molecule riboswitch inducers - MeiraGTx
Alternative Names: Riboswitch inducible anticancer programmes - MeiraGTxLatest Information Update: 28 Dec 2025
At a glance
- Originator MeiraGTx
- Class Antineoplastics; Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Unspecified
- No development reported Cancer
Most Recent Events
- 28 Dec 2025 No recent reports of development identified for preclinical development in Cancer in USA (Parenteral)
- 08 Jun 2023 Preclinical trials in Unspecified in USA (unspecified route) (MeiraGTx pipeline, June 2023)
- 12 Nov 2021 Preclinical trials in Cancer in USA (Parenteral) (MeiraGTx pipeline, November 2021)