Research programme: pharmacological chaperons - Protego Biopharma
Latest Information Update: 13 Aug 2025
At a glance
- Originator Protego Biopharma
- Class Small molecules
- Mechanism of Action Protein folding modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Achondroplasia; Myelofibrosis
Most Recent Events
- 13 Aug 2025 Early research in Achondroplasia in USA (unspecified route), before August 2025 (Protego Biopharma pipeline, August 2025)
- 13 Aug 2025 Early research in Myelofibrosis in USA (unspecified route), before August 2025 (Protego Biopharma pipeline, August 2025)
- 17 Nov 2021 Early research in Metabolic disorders in USA (unspecified route)