AMA 005
Alternative Names: AMA-005Latest Information Update: 21 Dec 2021
At a glance
- Originator Amarna Therapeutics
- Class Antihaemorrhagics; Gene therapies
- Mechanism of Action Factor IX replacements; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Haemophilia B