Drug Profile

Research programme: protein-based therapies - Vertex Pharmaceuticals/Horizon Therapeutics

Latest Information Update: 28 Feb 2026

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At a glance

Orphan Drug Status

Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

No
New Molecular Entity Yes

28 Feb 2026 No recent reports of development identified for preclinical development in Autoimmune-disorders in USA (Parenteral)
28 Jan 2026 No recent reports of development identified for research development in Inflammation in USA
17 Jan 2022 Preclinical trials in Autoimmune disorders in USA (Parenteral) as of January 2022 (Horizon Therapeutics pipeline, January 2022)

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