Research programme: glycogen storage disorder gene therapies - Kriya Therapeutics
Latest Information Update: 02 Feb 2022
At a glance
- Originator Duke University
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Glycogen storage disease