GC 1130A
Alternative Names: GC-1130A; NP-3011; Recombinant human heparan N-sulfatase - GC Biopharma; rhHNSLatest Information Update: 18 Feb 2025
At a glance
- Originator GC Pharma
- Developer GC Biopharma
- Class Enzymes; Recombinant proteins
- Mechanism of Action N-sulfoglucosamine sulfohydrolase replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes - Mucopolysaccharidosis III
Highest Development Phases
- Phase I Mucopolysaccharidosis III
Most Recent Events
- 11 Feb 2025 Pharmacodynamics data from preclinical studies in Mucopolysaccharidosis III
- 31 Oct 2024 Phase-I clinical trials in Mucopolysaccharidosis III (In children) in Japan (Intracerebral) (NCT06567769)
- 31 Oct 2024 Phase-I clinical trials in Mucopolysaccharidosis III (In children) in South Korea (Intracerebral) (NCT06567769)