Luspatercept analogue - Ionis Pharmaceuticals
Alternative Names: RAP-GRLLatest Information Update: 04 Feb 2022
At a glance
- Originator Ionis Pharmaceuticals
- Class Antianaemics; Disulfides; Immunoglobulin Fc fragments; Peptides; Recombinant fusion proteins
- Mechanism of Action TGF-beta superfamily protein inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Beta-thalassaemia