Research programme: anti-HTT oligonucleotides - Ceptur Therapeutics
Latest Information Update: 10 Feb 2022
At a glance
- Originator Ceptur Therapeutics
- Class Gene therapies; Oligonucleotides
- Mechanism of Action Huntingtin protein expression inhibitors; RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Huntington's disease
Most Recent Events
- 27 Jan 2022 Preclinical trials in Huntington's disease in USA (Parenteral) (Ceptur Therapeutics pipeline, January 2022)