M 021
Alternative Names: M-021Latest Information Update: 28 Mar 2026
At a glance
- Originator M6P Therapeutics
- Class Alpha-glucosidases; Enzymes; Recombinant proteins
- Mechanism of Action Alpha-glucosidase replacements; Enzyme replacements
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Glycogen storage disease type II
Most Recent Events
- 28 Mar 2026 No recent reports of development identified for preclinical development in Glycogen-storage-disease-type-II in USA
- 18 Jul 2025 M6P Therapeutics plans to submit IND for Glycogen storage disease type II by third quarter of 2026 (M6P Therapeutics pipeline, July 2025)
- 18 Jul 2025 Pharmacodynamics data from a preclinical trial in Pompe disease released by M6P Therapeutics (M6P Therapeutics pipeline, July 2025)