M 021
Alternative Names: M-021Latest Information Update: 13 Feb 2023
At a glance
- Originator M6P Therapeutics
- Class Alpha-glucosidases; Enzymes; Recombinant proteins
- Mechanism of Action Alpha-glucosidase replacements; Enzyme replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Glycogen storage disease type II
Most Recent Events
- 09 Feb 2023 M6P Therapeutics plans to submit IND for Glycogen storage disease type II by Q2 2024 (M6P Therapeutics website, February 2023)
- 09 Feb 2023 M 021 receives Rare pediatric drug status for Glycogen storage disease type II in USA prior to February 2023 (M6P Therapeutics website, February 2023)
- 10 Feb 2022 Pharmacodynamics data from preclinical trial presented at the 18th Annual WORLDSymposium™ (Annual WORLDSymposium-2022)