RTX 015
Alternative Names: RAY-001; RTX-015Latest Information Update: 06 Sep 2024
At a glance
- Originator Ray Therapeutics
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action Gene transference; Rhodopsin replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I Retinitis pigmentosa
- Preclinical Choroideraemia; Stargardt disease
Most Recent Events
- 31 Aug 2024 Phase-I clinical trials in Retinitis pigmentosa in USA (Intravitreous) (NCT06460844)
- 12 Jun 2023 Ray Therapeutics in-licenses AAV.7m8 intravitreal vector capsid from Adverum Biotechnologies
- 13 Apr 2023 Ray Therapeutics plans to initiate first-in-human clinical trials in Retinitis pigmentosa, by the end of 2023