CTx 001 - Complement Therapeutics
Alternative Names: CTx-001 - Complement TherapeuticsLatest Information Update: 13 Oct 2025
At a glance
- Originator University of Manchester
- Developer Complement Therapeutics
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Dry age-related macular degeneration
Most Recent Events
- 08 Oct 2025 US FDA approves IND application for CTx 001 in Dry-macular-degeneration
- 08 Oct 2025 Complement Therapeutics plans a phase I/II Opti-GAIN trial for Dry-macular-degeneration in the UK in first quarter of 2026 (Parenteral)
- 17 Apr 2023 Complement Therapeutics plans a phase Ib clinical proof of concept trial for Geographic atrophy